FDA approves Pfizer's first gene therapy for rare inherited bleeding disorder
FDA approves Pfizer's first gene therapy for rare inherited bleeding disorder
FDA approves Pfizer's first gene therapy for rare inherited bleeding disorder
The agency greenlit the drug, which will be marketed as Beqvez, for adults with moderate to severe hemophilia B who meet certain requirements.
The Food and Drug Administration on Friday approved Pfizer’s treatment for a rare genetic bleeding disorder, making it the company’s first-ever gene therapy to win clearance in the U.S.
The agency greenlit the drug, which will be marketed as Beqvez, for adults with moderate to severe hemophilia B who meet certain requirements.
The treatment will be available by prescription to eligible patients this quarter, a Pfizer spokesperson told CNBC. It has a hefty $3.5 million price tag, before insurance and other rebates, the spokesperson added, making it by far one of the most expensive drugs in the U.S.
Ooh, I think I remember reading somewhere that these patients have to be moved around insurance pools in the US just to keep the insurance industry working, lol. Because they're so expensive. I guess 3.5 is less than 20.
But, it's actually even so much better because it's supposed to work as a one time cure. So, in addition to smaller price tag all of the ongoing stress and coordination for the patients and the system just evaporates! So wonderful if it works.