FDA approves cure for sickle cell disease, the first treatment to use gene-editing tool CRISPR
FDA approves cure for sickle cell disease, the first treatment to use gene-editing tool CRISPR
www.reuters.com US approves two gene therapies for sickle cell disease
Sickle cell disease is a painful, inherited blood disorder that affects an estimated 100,000 people in the United States, most of whom are Black.
